Gene Therapy Advancements for Rare Genetic Disorders: Clinical, Ethical, and Regulatory Challenges. Nova Integrata: Journal of Multidisciplinary Studies, [S. l.], v. 1, n. 2, p. 20–35, 2023. Disponível em: https://nijms.online/index.php/journal/article/view/35. Acesso em: 14 apr. 2026.