[1]
“Gene Therapy Advancements for Rare Genetic Disorders: Clinical, Ethical, and Regulatory Challenges”, Nova Integrata J. Multidiscip. Stud., vol. 1, no. 2, pp. 20–35, Dec. 2023, Accessed: Apr. 14, 2026. [Online]. Available: https://nijms.online/index.php/journal/article/view/35